Goals, Mission & Vision h1 >
The mission of the Consortium is to maintain a clinical research network to study rare suppurative diseases of the airways, focusing on primary ciliary dyskinesia (PCD) and primary immunodeficiencies (PID).
The consortium consists of eight primary sites across North America.
The GDMCC works closely with several Patient Advocacy Groups, the larger Rare Diseases Clinical Research Consortium, and investigators/trainees at other clinical and academic centers. A major focus of our mission is to raise awareness of these disorders in the general public and educate policymakers, improve recognition of these disorders by physicians, and to train future generations of physicians and scientists who will lead and continue to advance rare disease research.
All Consortium sites have expertise in studying genetics and pathogenesis of airway diseases, clinical trial design, and development of novel therapeutics for defective lung defenses. In this proposal, we will develop collaborative, intellectual, and methodological resources for the study of rare diseases of the airways. Finally, the consortium plans to establish training programs in rare airways diseases and develop regional and internet-based networks to provide information about such rare diseases to the patients, medical professionals, and the lay public for education, referral, and recruitment of study subjects.
GDMCC Works To
- Raise awareness of these disorders in the general public and educate policymakers
- Improve recognition of these disorders by physicians
- Train future generations of physicians and scientists